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Overcoming Patient Recruitment Challenges in Rare Disease Trials

Rare diseases are thought to affect up to 446 million people worldwide. With more than 7,000 rare diseases, most of which are genetic, it’s vital all patients can access new and effective treatments.We know patient recruitment can be challenging even for non-complex trials, but this issue is exacerbated for rare disease studies due to the much smaller patient populations involved. This can lead to lengthy delays in bringing what can be cutting-edge and potentially life-changing therapies to market.With the global rare disease market expected to be worth more than US$547 billion within the next 10 years overcoming these challenges is critical. This webinar will:explore some of the patient recruitment challenges in rare disease studies, particularly relating to sickle cell trialshear from a patient and family member about what it means to live with a rare disease and highlight strategies to accelerate patient recruitment for these specialized trials.Learning ObjectivePatient recruitment challenges in rare disease studiesChallenges in sickle cells studiesFamily/Patient perspectiveAccelerating patient recruitment in rare disease studiesSpeaker 1 – Whitney Taynton – Business Unit Head, Site Enrollment Optimization, Innovative TrialsSpeaker 2 – Donna Dail – Director, Patient Recruitment Programs (Rare Disease)Speaker 3 – Margaret Alege – Patient


This content was provided by Innovative Trials

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