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Dietary Management

- PMLiVE

Sobi receives NICE recommendation for Altuvoct in severe haemophilia A

Approximately 7,700 people in England are living with the genetic bleeding disorder

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MHRA approves Galderma’s Nemluvio to treat atopic dermatitis and prurigo nodularis

The drug has been authorised to treat patients with moderate-to-severe cases of the skin diseases

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The full potential of patient journeys in pharma

Unlocking three actions to take now

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Navigating market access: Launch strategies and health economic modelling for medical devices – a live panel discussion

Discover how health economics can support successful Medical Device launch, proposition development, and market access. Join us live at 1:30pm (GMT) on Wednesday 19th March for an insightful journey into...

Petauri Evidence

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Rare diseases: Novartis’ Fabhalta recommended by CHMP for C3 glomerulopathy

Approximately one to two people per million worldwide are diagnosed with the ultra-rare kidney disease every year

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Rare diseases: CHMP recommends Krystal’s Vyjuvek for dystrophic epidermolysis bullosa

There is currently only one treatment authorised for the ultra-rare genetic blistering disease

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Key clinical trial trends – EU vs US perspectives

Highlighting the distinct priorities and hurdles faced by sponsors, CROs and sites around the world

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Rare Disease Day 2025 – highlighting recent approvals in the rare disease space

There are more than 7,000 known rare diseases that impact 300 million people globally

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Researchers discover previously unidentified genes linked to rare diseases

Up to 80% of rare disease patients remain undiagnosed after genomic sequencing

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Defying the odds: speeding patient access to life-changing treatments in rare disease

To deliver treatments for rare diseases more quickly, companies share how they are adapting their launch strategies and engaging more deeply with physicians and experts

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Astrategia

Strategy blindness is a thing

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Medscape’s Impact on Women’s Health Education: Key Publications at ISSWSH 2025 & Beyond

Just in time for Women’s History Month and International Women’s Day on March 8th, Medscape is proud to showcase its dedication to advancing women's health education. Sara Thorpe, MPH, Director,...

Medscape Education

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