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orphan diseases

- PMLiVE

Smarter Learning and Better Outcomes: How AI Can Provide an Advantage in Medical Education

See how AI-powered patient avatars allow physicians to test complex diagnoses and treatment plans in a simulated environment.

Impetus Digital

- PMLiVE

Lundbeck completes patient randomisation for phase 3 trial for multiple system atrophy treatment

The rare neurodegenerative disorder has no cure and no approved treatments

- PMLiVE

Data, Evidence, Education: Tackling the Global Multi‑Trillion‑Dollar Rare Disease Burden

Rare diseases are individually uncommon, yet together they affect an estimated 300 million+ people worldwide and touch the lives of over one billion when families and caregivers are included. For...

Medscape Education

phthalmologist, optometrist checking child, little girl vision looking for problems and caring for eye

Why patient engagement must come first in rare disease trials

Explore why patient engagement is the cornerstone of successful rare disease trials, emphasising the importance of designing studies around the realities of patients' lives to build trust and improve outcomes.

Cuttsy + Cuttsy

- PMLiVE

#ShortenTheJourney

For the millions of people living with a rare disease, the path to a diagnosis (if ever received) is often a long and frustrating odyssey. This delay is frequently driven...

Medscape Education

- PMLiVE

New Webinar: 2026 Engagement Strategies For Modern Pharma

Turn interaction into intelligence! Don’t miss this chance to lead the industry with our free pharma-exclusive webinar!

Impetus Digital

- PMLiVE

Women Leaders Rewriting the Protocols of Rare Disease Care

The true measure of a medical leader is the courage to act when existing systems fail the patient. This is the professional and personal ethos of clinical immunologist Dr. Hilary...

Medscape Education

- PMLiVE

Medscape Wins Anthem Award for Rare Disease Education Platform

Platform has reached 2.4 million healthcare professionals worldwide since 2021. Newark, NJ - [November 18, 2025] - Medscape, the leading digital platform for physicians and healthcare professionals (HCPs), has been...

Medscape Education

- PMLiVE

Learn the golden standard for omnichannel strategies!

Tired of a fragmented omnichannel strategy that falls short of its promise? Join our free webinar to learn how to eliminate silos and turn fragmented data into actionable insights. Register...

Impetus Digital

- PMLiVE

Your Blueprint for Flawless Pharma Omnichannel

Learn how to eliminate silos, transform data into actionable insights, and drive unparalleled efficiency across your key initiatives. Secure your spot in our free webinar, exclusive for life science professionals!

Impetus Digital

Build a KOL Community Virtually – Engaging Your Advisors Creatively

Go beyond formal meetings! Discover a creative way to build a virtual KOL community through ongoing discussion forums. Facilitate peer-to-peer best practice sharing and foster authentic, sustained relationships with your...

Impetus Digital

Streamline Clinical Trial Collaboration – Engaging Your Advisors Creatively

Boost efficiency in clinical operations! Learn a creative way to enhance communication between teams at different sites and streamline the development of study protocols, support materials, and journal submissions.

Impetus Digital

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