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- PMLiVE

patient advocates

Genentech’s Sunil Agarwal joins rare disease firm

He will serve as chief medical officer at Ultragenyx

- PMLiVE

FDA approves drug for rare swelling diseases

Salix and Pharming’s Ruconest is made from the milk of genetically-modified rabbits

- PMLiVE

Channel strategy and orphan drugs

A plan for guiding decisions about a product's distribution channel is particularly relevant for orphan drugs, rare diseases or specialty medicines

- PMLiVE

FDA sets out framework for rare childhood diseases

Wants to encourage more trial use of biomarkers and speedier approval timelines

- PMLiVE

The moving parts of orphan drug development

Tackling rare diseases requires high levels of cooperation, regulatory support and a determination to succeed

- PMLiVE

FDA gives early green light to Spectrum’s lymphoma drug

Beleodaq approved to treat rare cancer

Changing behaviour – appealing to the rational and emotional mind

Elisa Del Galdo, Head of Customer Experience here at Blue Latitude, talks about how to understand what motivates your customer and influence their behaviour, prompting a change in behaviour which...

Blue Latitude Health

The key to designing great digital services in healthcare

Fred Bassett, co-founder and Head of Strategy at Blue Latitude, talks about the key to designing great digital services in healthcare.

Blue Latitude Health

- PMLiVE

Otsuka launches European ADPKD forum

Aims to lead awareness raising plans for rare genetic condition

- PMLiVE

EC approves Janssen rare blood disorder drug

Sylvant available to treat multicentric Castleman's disease

- PMLiVE

The digital transformation of market research

How technology is bringing new clarity to the patient voice

Shire Basingstoke

Shire boosts rare disease portfolio with $260m Lumena deal

Acquisition of US company will bring two mid-stage candidates for rare liver diseases

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