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- PMLiVE

patient advocates

Biomarin

EC approves Biomarin rare genetic disorder drug

Vimizim now available to treat Morquio A syndrome

- PMLiVE

FDA approves Janssen drug for rare Castleman’s disease

Sylvant approved to treat lymphoma-like condition

- PMLiVE

BioAlliance and Topotarget merge to focus on rare cancers

French and Danish firms combine to develop orphan oncology drugs

- PMLiVE

EU and Australian regulators collaborate on rare diseases

EMA and Therapeutic Goods Administration to share reports for orphan drugs

- PMLiVE

Developing your patient-centric strategy

How to succeed when your vehicle of engagement is not a disease

- PMLiVE

Sanofi appoints ‘chief patient officer’

Dr Anne Beal will lead pharma company’s efforts to improve its focus on patients

- PMLiVE

Online Parkinson’s platform could revolutionise chronic disease care

ParkinsonNet connects patients with doctors in a virtual setting

- PMLiVE

Final NICE backing for MabThera in rare condition

Roche drug available in England and Wales to treat rare form of vasculitis

- PMLiVE

Pharma needs to be “revered by society”

Janssen’s Jane Griffiths and EFPIA chief Richard Bergstrom speak at eyeforpharma conference

- PMLiVE

No price ceiling for rare disease drugs, say MPs

BIA survey comes ahead of consultation on evaluation framework for ultra-orphans

NICE and ‘ultra orphans’

NICE and its processes for ‘highly specialised therapies’

EU flag

J&J gets EU green light for novel TB drug

Sirturo approved to treat multidrug resistant form of the disease

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