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- PMLiVE

PureTech’s deupirfenidone gets FDA and EC Orphan Drug Designations for idiopathic pulmonary fibrosis

Rare diseases are defined as conditions affecting fewer than 200,000 people in the US or fewer than five in 10,000 individuals in the European Union

- PMLiVE

CGT Catapult establishes Technology Advisory Board led by chair Phil Vanek

The board will support the CGT Catapult in identifying and removing barriers to the widespread adoption of advanced therapies

- PMLiVE

Diabeloop’s DBLG2 receives FDA and CE clearance for automated insulin delivery without meal input

While a lack of meal announcements can lead to lower glycaemic control, it reduces the mental burden for those with type 1 diabetes

- PMLiVE

Human Continuum appoints Omar Khalid Sial as Chief Scientific Officer

Sial has authored multiple peer-reviewed publications for major journals

- PMLiVE

#ShortenTheJourney

For the millions of people living with a rare disease, the path to a diagnosis (if ever received) is often a long and frustrating odyssey. This delay is frequently driven...

Medscape Education

- PMLiVE

British Chambers of Commerce partners with Singapore to scale up UK imports

The Singapore Life Sciences Trade Accelerator six-month pilot programme aims to increase export opportunities

- PMLiVE

The PM Society launches Pharmony to support more effective pharma-agency collaboration

The not-for-profit membership organisation represents healthcare professionals in the UK

- PMLiVE

Communication breakdown

Why soft skills are more important than ever in life sciences

- PMLiVE

Why We Must Stop Normalizing the “Pregnancy Itch”

In the world of rare diseases, success is often measured by the speed of diagnosis. However, for women facing rare liver conditions like Intrahepatic Cholestasis of Pregnancy (ICP), the medical...

Medscape Education

- PMLiVE

UCB’s Kygevvi receives positive CHMP opinion for thymidine kinase 2 deficiency

TK2d is an extremely rare disease characterised by severe and progressive muscle weakness

- PMLiVE

THX Pharma appoints Julien Veys as Deputy CEO

Veys has served at THX for almost a decade, including as Chief Operating Officer

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