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- PMLiVE

Publicis Health UK promotes Katie McMorran and Clare Middleton as Langland group managing directors

McMorran will lead the agency's advertising practice and Middleton will head the clinical trial experience, medical strategy and education, and public relations disciplines

- PMLiVE

Women in pharma

With February marking the International Day of Women and Girls in Science, Iona Everson from PMGroup spoke to Emma Banks, CEO of ramarketing, to find out more about her career

- PMLiVE

UKRI appoints iiCON to deliver £1.5m initiative to tackle infection transmission

The project will aim to accelerate solutions that leverage technologies such as AI and novel diagnostics

- PMLiVE

FDA awards Orphan Drug Designation to SynaptixBio for rare brain disease therapy

Isolated hypomyelination is a form of TUBB4A leukodystrophy that has been identified relatively recently

- PMLiVE

Sanofi presents positive results for rilzabrutinib in chronic spontaneous urticaria

Phase 3 development of the treatment is expected to commence later this year

- PMLiVE

Radboud researchers use new method to improve diagnosis of rare diseases

Approximately 7,000 rare diseases collectively impact up to 5.9% of the global population

- PMLiVE

OneChain-led consortium granted €1.9m to advance CAR-T therapy for rare leukaemia

Acute lymphoblastic leukaemia has an incidence of around 1.5 cases per 100,000 people

- PMLiVE

Clinigen launches ‘What is Possible?’ campaign on Rare Disease Day to accelerate access to medicines

There are over 7,000 rare diseases impacting more than 300 million people globally

- PMLiVE

CHMP recommends Travere and CSL Vifor’s Filspari to treat rare kidney disease IgAN

The rare form of kidney disease is estimated to affect around 25 per million adults worldwide

- PMLiVE

The pharma trailblazer’s skill set: forged in rare diseases

There is one very special, overlooked area, in large organisations and small, that builds skills like no other: rare diseases

- PMLiVE

Rare diseases – driving further improvements in patient access

Despite significant strides, many rare disease patients have no licensed treatment options and face high levels of unmet need

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