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UniQure

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Gene therapy market access Q&A

Jesper Jorgensen, Health Economics and Market Access Manager, Cell and Gene Therapy Catapult gives his personal view on how to get the new therapies to patients

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Novartis builds case for SMA gene therapy as FDA verdict looms

One shot therapy provided rapid improvement in motor function

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UniQure gets speedy US review for Huntington’s gene therapy

Pioneer gaining momentum again

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Sangamo surges on data for haemophilia A gene therapy

After recent setbacks, news lifts shares

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UniQure edges closer to haemophilia B gene therapy OK

The candidate could free patients from regulator injections of FIX products

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J&J bolsters gene therapy unit with $100m MeiraGTx deal

Licenses two inherited retinal disorder candidates

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UniQure cleared to start Huntington gene therapy trial

AMT-130 becomes the first AAV-based therapy approved for trials in Huntington’s disease

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UniQure skyrockets on haemophilia B gene therapy data

Competition with Pfizer and Spark rival heats up

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Encouraging data for GenSight’s blinding retinal disease gene therapy

Better results after April's setback

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Orchard plans IPO as gene therapy pipeline advances

UK biotech seeks funds for expanded rare disease portfolio

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EMA to review Bluebird’s blood disorder gene therapy

LentiGlobin could free patients of regular blood transfusions

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Sangamo bulks up in cell therapy with TxCell acquisition

Hopes to start cell-based immunotherapy trials next year

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