
The study demonstrated meaningful survival benefits for patients with cutaneous T cell lymphoma

The phase 3 study included around 2,600 patients

The inflammatory skin disease affects up to 20% of children and 10% of adults worldwide

XLH is a life-long genetic disease that causes abnormalities in the bones, muscles and joints

Results of eight main studies of drug were 'inconsistent', according to the CHMP

Drug is being reviewed under new ultra-orphan pathway

Watchdog to back the drug to treat young people with XLH

Becomes the first drug approved to treat Sézary syndrome

Committee says the rare disease therapy isn’t value for money