peripheral artery disease
AL-S Pharma release new data from AP-101 phase 2 trial for ALS
ALS is a progressive neurodegenerative disease that affects the motor neurons of the brain and spinal cord
Astellas’ application to EMA validated for treatment of muscle-invasive bladder cancer
Bladder cancer affects over 224,000 people annually in Europe, with over 30% of cases being muscle-invasive bladder cancer
Novartis’ Itvisma gets FDA approval for spinal muscular atrophy treatment
Around 9,000 people in the US currently live with SMA
Roche’s Evrysdi tablets approved by MHRA to treat spinal muscular atrophy
It is hoped the new formulation will offer patients greater freedom and flexibility compared to the liquid version
Biogen’s Qalsody granted MHRA approval to treat rare form of motor neurone disease
Mutations in the SOD1 gene are responsible for approximately 2% of all cases of the disease
Roche’s Evrysdi tablets granted EC approval to treat spinal muscular atrophy
The neuromuscular disease affects approximately one in every 10,000 babies worldwide
Cytokinetics shares positive phase 3 results for aficamten in heart disease
Up to one in 500 people in the UK and US are living with hypertrophic cardiomyopathy
Eli Lilly and Alchemab Therapeutics enter ALS agreement worth up to $415m
The deal follows the companies’ earlier partnership to advance candidates for the neurodegenerative disease
Novartis shares positive phase 3 results for spinal muscular atrophy gene therapy
The company said it is planning to file regulatory applications for OAV101 IT this year
Roche’s Evrysdi tablet formulation granted FDA approval for spinal muscular atrophy
The progressive neuromuscular disease affects approximately one in every 10,000 babies globally
Biogen’s higher dose spinal muscular atrophy regimen accepted for review by EMA/FDA
The neuromuscular disease affects approximately one in every 10,000 babies worldwide
Eli Lilly and Alchemab Therapeutics partner to develop new ALS therapies
The neurodegenerative disease affects approximately 30,000 people in the US