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TechnologyAdvice

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US FDA launches ultra-rare diseases framework

The draft guidance specifically discusses genome editing and RNA-based therapies

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N4 Pharma appoints David Solomon as CEO

The company is to be renamed Thalia Therapeutics to reflect its strategic transition

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Why stigma is a launch risk in rare disease – and what commercial leaders can do about it

Rare disease launches are complex by nature. Yet one of the most consistent risks we see is rarely treated as a launch issue at all: stigma.

Havas Life London

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New report identifies stigma as a structural barrier in rare disease

The study finds that healthcare settings are a leading source of stigma for people living with rare conditions

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Patient-centricity in rare disease: accelerating the path to treatment

By Chris Moore

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GenAI in healthcare: why privacy and literacy matter more than the tech

By Dimitri Challouma

Involvement of children and young people in research and publication development

From ‘why’ to ‘how’: patient partnership across age groups in research and publications

By Sarah Mohamad

Amiculum

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From Static to Strategic: The 2026 Playbook for Longitudinal Pharma Interaction

Stop pushing content at a burnt-out audience and start creating "Digital Magnetism." Join Impetus Digital to unlock the 2026 Engagement Toolkit—a deep dive into the immersive, longitudinal strategies and newly...

Impetus Digital

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Novo Nordisk and Vivtex partner in deal worth up to $2.1bn

The companies aim to develop next-generation oral medicines for obesity and diabetes

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AI-enabled, human-interpreted: the future of pharma marketing insights is precision intelligence

By Abigail Stuart

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It’s time for an end to pharma exceptionalism

By Mark Ralphs

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Data, Evidence, Education: Tackling the Global Multi‑Trillion‑Dollar Rare Disease Burden

Rare diseases are individually uncommon, yet together they affect an estimated 300 million+ people worldwide and touch the lives of over one billion when families and caregivers are included. For...

Medscape Education

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